This is an open-label extension study for patients who complete a Phase 3, placebo-controlled study of ataluren in patients with nonsense mutation cystic fibrosis (nmCF) not receiving chronic inhaled aminoglycosides.
A Phase 3 Extension Study of Ataluren (PTC124) in Patients With Nonsense Mutation Cystic Fibrosis
You can join if…
Open to people ages 6 years and up
Completion of study treatment (placebo or active) in the previous Phase 3,double-blind study protocol (Protocol PTC124-GD-021-CF)
You CAN'T join if...
Ongoing participation in any other therapeutic clinical trial
Children's Hospital and Research Center at Oakland Oakland, California, 94609, United States
Stanford University-Children's Hospital Palo Alto, California, 94304, United States
Children's Hospital Los Angeles Los Angeles, California, 90027, United States
Miller Children's Hospital Long Beach Long Beach, California, 90806, United States