Nervous System Diseases clinical trials at UCSF

• Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy

  open to eligible males ages 5 years and up

  This study is a long-term study of ataluren in participants with nonsense mutation Duchenne muscular dystrophy.

  Oakland, California and other locations

• Safety and Efficacy Study of VY-AADC01 for Advanced Parkinson's Disease

  Sorry, in progress, not accepting new patients

  Safety and efficacy of AADC gene transfer in participants with Parkinson's disease.

  San Francisco, California and other locations

Last updated: September 2, 2020