Neuromuscular Diseases clinical trials at UCSF
2 in progress, 0 open to eligible people
A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy
Sorry, not currently recruiting here
This trial will study the efficacy and safety of taldefgrobep alfa as an adjunctive therapy for participants who are already taking a stable dose of nusinersen or risdiplam or have a history of onasemnogene abeparvovec-xioi, compared to placebo.
San Francisco, California and other locations
Sorry, in progress, not accepting new patients
This study is a long-term study of ataluren in participants with nonsense mutation Duchenne muscular dystrophy.
Oakland, California and other locations
Our lead scientists for Neuromuscular Diseases research studies include Jonathan Strober.