Skip to main content

PFIC1 clinical trials at UCSF
1 research study open to eligible people

  • This Study Will Investigate the Efficacy and Safety of A4250 in Children With PFIC 1 or 2

    open to eligible people ages 6 months to 18 years

    Double blind, randomized, placebo controlled, Phase 3 study to investigate the efficacy and safety of low doses and high doses of A4250 compared to placebo in children with PFIC (deficiencies of familial intrahepatic cholestasis-1 or bile salt export pump).

    San Francisco, California and other locations

Last updated: