Skip to main content

AADC Deficiency clinical trials at UCSF

1 research study open to eligible people

AADC deficiency is a rare genetic disorder affecting the brain. UCSF is conducting trials to test new treatments for children with this condition. These trials examine the safety and effectiveness of a gene therapy that delivers the AADC enzyme to the brain.

Showing trials for

Our lead scientists for AADC Deficiency research studies include .

Last updated: