Achondroplasia clinical trials at UCSF
4 in progress, 0 open to new patients

• A Clinical Trial to Evaluate the Safety and Efficacy of BMN 111 in Infants and Young Children With Achondroplasia

  Sorry, accepting new patients by invitation only

  Study 111-206 is a Phase 2 randomized, double-blind, placebo-controlled clinical trial of BMN 111 in infants and young children with a diagnosis of Achondroplasia.

  Oakland, California and other locations

• A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients With Achondroplasia

  Sorry, accepting new patients by invitation only

  Multicenter, multinational study to collect consistent baseline growth measurements on pediatric patients with Achondroplasia being considered for subsequent enrollment in future studies sponsored by BioMarin. No study drug is administered.

  Oakland, California and other locations

• A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH)

  Sorry, in progress, not accepting new patients

  This is a Phase 2, Open-Label, Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of BMN 111 in Children with Achondroplasia. The primary objective is to evaluate the long-term safety and tolerability of daily SC injections of BMN 111 in children with ACH who have completed two years of treatment in the 111-202 study.

  Oakland, California and other locations

• A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia

  Sorry, in progress, not accepting new patients

  The intent and design of this Phase 3 study is to assess BMN 111 as a therapeutic option for the treatment of children with Achondroplasia.

  Oakland, California and other locations

Last updated: January 15, 2019