Alpha Thalassemia clinical trials at UCSF
3 in progress, 1 open to eligible people
Alpha thalassemia is a blood disorder that affects the body's ability to produce hemoglobin. UCSF is recruiting for studies to learn more about this disease and its effects on patients. These trials will help gather important information about the health and outcomes of those with alpha thalassemia.
International Registry of Patients With Alpha Thalassemia
open to all eligible people
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
San Francisco, California
Mitapivat in Participants with Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or Β-TDT)
Sorry, in progress, not accepting new patients
The primary purpose of this study is to compare the effect of mitapivat versus placebo on transfusion burden in participants with transfusion-dependent alpha- or beta-thalassemia (TDT).
Oakland, California and other locations
In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM)
Sorry, accepting new patients by invitation only
The investigators aims to evaluate the safety of in utero hematopoietic stem cell transplantation in fetuses with alpha-thalassemia major performed at the time of in utero transfusion of red blood cells.
San Francisco, California
Our lead scientists for Alpha Thalassemia research studies include Tippi C MacKenzie, MD.
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