Alpha Thalassemia clinical trials at UCSF
2 in progress, 1 open to eligible people
Alpha thalassemia is an inherited condition that limits red blood cell production. UCSF is maintaining an international registry that gathers medical and pregnancy data from patients. UCSF is running observational studies that record symptoms and lab findings over time.
International Registry of Patients With Alpha Thalassemia
open to all eligible people
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
San Francisco, California
Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
Sorry, in progress, not accepting new patients
The primary objective of this study was to compare the effect of mitapivat versus placebo on transfusion burden in participants with α- or β-transfusion-dependent thalassemia.
Oakland, California and other locations
Our lead scientists for Alpha Thalassemia research studies include Tippi C MacKenzie, MD.
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