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Alpha Thalassemia Major clinical trials at UCSF

3 in progress, 2 open to eligible people

Alpha thalassemia major is a blood disorder that causes anemia. UCSF is conducting clinical trials to explore treatments for this condition. One trial involves creating an international registry to learn more about the disease and fetal therapy outcomes. Another trial is testing the safety and effectiveness of a treatment called EDIT-301 in adult participants with the disease.

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Our lead scientists for Alpha Thalassemia Major research studies include .

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