ATTRv-PN clinical trials at UCSF
1 research study open to eligible people
ATTRv-PN is an inherited condition where transthyretin protein builds up and damages nerves. UCSF is running a study that follows people over months and years to note changes. UCSF is recording exams, lab tests, and patient symptoms for research files.
Patients With Transthyretin (ATTR) Amyloidosis
open to eligible people ages 18-130
The MaesTTRo study aims to enroll a global cohort of patients with transthyretin (ATTR) amyloidosis to longitudinally observe the natural course of the disease and describe real-world treatment patterns and outcomes. In addition, information on the effectiveness of ATTR amyloidosis treatments, including eplontersen, which is a ligand-conjugated antisense oligonucleotide gene silencing treatment targeting activity against both the mutant and wild-type TTR protein, will be collected.
San Francisco, California and other locations
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