Blindness clinical trials at UCSF

1 research study open to eligible people

Blindness means a person has severe vision loss that limits daily life. UCSF is studying eye gene therapy, drug injections, and imaging tests for retinal disease. Some research compares one eye to the other using randomized, masked methods.

Showing trials for

  • Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

    open to eligible people ages 6 years and up

    The purpose of this double-masked, randomized, placebo-controlled, paired-eye study is to evaluate the efficacy, safety and tolerability of Sepofarsen in subjects with Leber Congenital Amaurosis (LCA) due to the c.2991+1655A>G (p.Cys998X) mutation in the CEP290.

    San Francisco, California and other locations

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