Canavan Disease clinical trials at UCSF

1 research study open to eligible people

Canavan Disease is a rare illness. UCSF has a clinical trial for it. This trial is testing a new gene therapy called BBP-812. The main goal is to make sure it is safe and acceptable for patients with Canavan Disease.

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  • AAV9 Gene Therapy in Participants With Canavan Disease

    open to eligible people ages up to 30 months

    The main objective of this trial is to evaluate the safety, tolerability, and pharmacodynamic activity of BBP-812, an investigational AAV9-based gene therapy, in pediatric participants with Canavan disease.

    Oakland, California and other locations

Our lead scientists for Canavan Disease research studies include .

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