Cone-Rod Dystrophy clinical trials at UCSF

1 research study open to eligible people

Cone-rod dystrophy is an eye disorder affecting vision due to damaged light-sensing cells. UCSF is conducting trials to investigate a new medicine for Stargardt disease caused by ABCA4 gene problems. Participants receive varying doses to assess safety and effectiveness.

Showing trials for

  • ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR)

    open to eligible people ages 18 years and up

    This study is an open-label, single ascending dose clinical trial in participants who have ABCA4-related retinopathies. This is the first-in-human clinical trial in which ACDN-01 will be evaluated for safety, tolerability, and preliminary efficacy following a single subretinal injection of ACDN-01.

    San Francisco, California and other locations

Our lead scientists for Cone-Rod Dystrophy research studies include .

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