Congenital Adrenal Hyperplasia clinical trials at UCSF
2 in progress, 1 open to eligible people
open to eligible people ages 18 years and up
This is a Phase 3 study to evaluate the efficacy, safety, and tolerability of crinecerfont versus placebo administered for 24 weeks in approximately 165 adult participants with classic CAH due to 21-hydroxylase deficiency. The study consists of a 6-month randomized, double-blind, placebo-controlled period, followed by 1 year of open-label treatment with crinecerfont. Subsequently, participants may elect to participate in the open-label extension (OLE) period. The duration of participation in the study is approximately 20 months for the core study and will be a variable amount of time per subject for the OLE (estimated to be approximately 3 years).
San Francisco, California and other locations
Sorry, not currently recruiting here
This study is designed to evaluate the safety, tolerability, and efficacy of AAV5 based BBP-631 in adult participants diagnosed with classic congenital adrenal hyperplasia.
Oakland, California and other locations
Our lead scientists for Congenital Adrenal Hyperplasia research studies include Paul Harmatz, MD.