Congenital Adrenal Hyperplasia clinical trials at UCSF

2 in progress, 1 open to eligible people

Showing trials for

  • Global Safety and Efficacy Registration Study of Crinecerfont for Congenital Adrenal Hyperplasia

    open to eligible people ages 18 years and up

    This is a Phase 3 study to evaluate the efficacy, safety, and tolerability of crinecerfont versus placebo administered for 24 weeks in approximately 165 adult participants with classic CAH due to 21-hydroxylase deficiency. The study consists of a 6-month randomized, double-blind, placebo-controlled period, followed by 1 year of open-label treatment with crinecerfont. Subsequently, participants may elect to participate in the open-label extension (OLE) period. The duration of participation in the study is approximately 20 months for the core study and will be a variable amount of time per subject for the OLE (estimated to be approximately 3 years).

    San Francisco, California and other locations

  • A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)

    Sorry, not currently recruiting here

    This study is designed to evaluate the safety, tolerability, and efficacy of AAV5 based BBP-631 in adult participants diagnosed with classic congenital adrenal hyperplasia.

    Oakland, California and other locations

Our lead scientists for Congenital Adrenal Hyperplasia research studies include .

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