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Hemoglobinopathy clinical trials at UCSF

3 in progress, 2 open to eligible people

Hemoglobinopathy is a condition that affects the blood and can cause anemia. At UCSF, we are running trials to test treatments for severe sickle cell disease and beta thalassemia. In these trials, we will look at the safety and effectiveness of EDIT-301, a treatment that uses the patient's own stem cells to produce healthy blood cells. Participants must be adults and will be closely monitored throughout the trials.

Showing trials for

Our lead scientists for Hemoglobinopathy research studies include .

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