Neurological Manifestations clinical trials at UCSF
1 research study open to eligible people
Neurological manifestations are signs or symptoms caused by nervous system problems. UCSF is running clinical studies for brain, spine, and nerve conditions. One study gives a drug to one eye and a placebo to the other in a blinded test for inherited retinal disease.
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Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
open to eligible people ages 6 years and up
The purpose of this double-masked, randomized, placebo-controlled, paired-eye study is to evaluate the efficacy, safety and tolerability of Sepofarsen in subjects with Leber Congenital Amaurosis (LCA) due to the c.2991+1655A>G (p.Cys998X) mutation in the CEP290.
San Francisco, California and other locations
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