Neurological Manifestations clinical trials at UCSF

1 research study open to eligible people

Neurological manifestations refer to symptoms linked with disorders of the nervous system. UCSF is running trials to evaluate Sepofarsen in individuals with specific vision issues like Leber Congenital Amaurosis. These studies help researchers test new treatments for nervous system-related conditions.

Showing trials for

  • Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

    open to eligible people ages 6 years and up

    The purpose of this double-masked, randomized, placebo-controlled, paired-eye study is to evaluate the efficacy, safety and tolerability of Sepofarsen in subjects with Leber Congenital Amaurosis (LCA) due to the c.2991+1655A>G (p.Cys998X) mutation in the CEP290.

    San Francisco, California and other locations

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