PIK3CA-Related Overgrowth Spectrum clinical trials at UCSF

1 research study open to eligible people

Study Assessing the Efficacy, Safety and PK of Alpelisib (BYL719) in Pediatric and Adult Patients With PIK3CA-related Overgrowth Spectrum
open to eligible people ages 2 years and up
This is a prospective Phase II multi-center study with an upfront 16-week, randomized, double-blind, placebo-controlled period, and extension periods, to assess the efficacy, safety and pharmacokinetics of alpelisib in pediatric and adult participants with PIK3CA-related overgrowth spectrum (PROS).
San Francisco, California and other locations

Our lead scientists for PIK3CA-Related Overgrowth Spectrum research studies include Beth Apsel Winger.

Last updated: May 15, 2023

Study Assessing the Efficacy, Safety and PK of Alpelisib (BYL719) in Pediatric and Adult Patients With PIK3CA-related Overgrowth Spectrum