Sandhoff Disease clinical trials at UCSF

1 in progress, 0 open to eligible people

GM1 and GM2 Gangliosidosis PROspective Neurological Disease TrajectOry Study (PRONTO)
Sorry, in progress, not accepting new patients
The study aims to characterize prospectively longitudinal progression of neurological domains in GM1 and GM2 Gangliosidosis patients with high-quality standards (GCP compliant).
Oakland, California and other locations

Last updated: October 2023