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Sandhoff Disease clinical trials at UCSF

1 research study open to eligible people

Sandhoff Disease is a rare genetic disorder that affects the nervous system. UCSF is recruiting patients for a clinical trial called PRONTO. This trial aims to track how Sandhoff Disease progresses in patients over time, specifically in terms of neurological symptoms. Joining this trial can help researchers understand the disease better and improve treatments in the future.

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Our lead scientists for Sandhoff Disease research studies include .

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