Tay-Sachs Disease clinical trials at UCSF
1 research study open to eligible people
Tay-Sachs Disease is a genetic disorder that affects the nervous system. UCSF is now recruiting for a clinical trial called "PRONTO". This trial studies how the disease progresses in patients with GM1 and GM2 forms of Tay-Sachs Disease. The goal is to better understand the disease and its effects on the nervous system.
open to eligible people ages 2-20
The study aims to characterize prospectively longitudinal progression of neurological domains in GM1 and GM2 Gangliosidosis patients with high-quality standards (GCP compliant).
Oakland, California and other locations
Our lead scientists for Tay-Sachs Disease research studies include Paul Harmatz, MD.