Thalassemia clinical trials at UCSF
3 in progress, 1 open to eligible people
Thalassemia is a genetic condition where the body makes less hemoglobin than normal. UCSF is conducting studies to see how thalassemia changes over a person's life. UCSF is researching the effects of existing therapies in treating thalassemia.
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
open to all eligible people
In parallel with the growth of American Thrombosis and Hemostasis Network's (ATHN) clinical studies, the number of new therapies for all congenital and acquired hematologic conditions, not just those for bleeding and clotting disorders, is…
Oakland, California and other locations
Etavopivat in Patients With Thalassemia or Sickle Cell Disease
Sorry, in progress, not accepting new patients
This clinical trial is a Phase 2 study that will evaluate the safety and clinical activity of etavopivat in patients with thalassemia or sickle cell disease and test how well etavopivat works to lower the number of red blood cell transfusions…
Oakland, California and other locations
Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia
Sorry, in progress, not accepting new patients
Study AG348-C-010 is a multicenter study to evaluate the efficacy, safety, pharmacokinetics, and pharmacodynamics of treatment with AG-348 in adult participants with non-transfusion-dependent thalassemia (NTDT). This study includes a core period (up …
Oakland, California and other locations
Our lead scientists for Thalassemia research studies include Alison Matsunaga, MD.
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