Alpha Thalassemia clinical trials at UCSF
2 in progress, 1 open to eligible people
Alpha thalassemia is a hereditary blood condition that causes low hemoglobin. UCSF is maintaining an international registry of patients to collect health and pregnancy data. The registry logs lab tests, clinic visits, and birth outcome records.
International Registry of Patients With Alpha Thalassemia
open to all eligible people
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
San Francisco, California
Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
Sorry, in progress, not accepting new patients
The primary objective of this study was to compare the effect of mitapivat versus placebo on transfusion burden in participants with α- or β-transfusion-dependent thalassemia.
Oakland, California and other locations
Our lead scientists for Alpha Thalassemia research studies include Tippi C MacKenzie, MD.
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