Alpha Thalassemia clinical trials at UCSF
2 in progress, 1 open to eligible people
Alpha thalassemia is a medical condition affecting the body's ability to produce hemoglobin. UCSF is gathering information worldwide from individuals with this condition. The goal is to document experiences and outcomes from fetal development onward.
International Registry of Patients With Alpha Thalassemia
open to all eligible people
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
San Francisco, California
Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
Sorry, in progress, not accepting new patients
The primary objective of this study was to compare the effect of mitapivat versus placebo on transfusion burden in participants with α- or β-transfusion-dependent thalassemia.
Oakland, California and other locations
Our lead scientists for Alpha Thalassemia research studies include Tippi C MacKenzie, MD.
Last updated: