Alpha Thalassemia clinical trials at UCSF
2 in progress, 1 open to eligible people
Alpha thalassemia is a blood disorder that affects hemoglobin production. UCSF is recruiting for a study to collect data on alpha thalassemia patients worldwide. This research aims to learn how the disease progresses and its effects on unborn babies.
International Registry of Patients With Alpha Thalassemia
open to all eligible people
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
San Francisco, California
Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
Sorry, in progress, not accepting new patients
The primary purpose of this study is to compare the effect of mitapivat versus placebo on transfusion burden in participants with transfusion-dependent alpha- or beta-thalassemia (TDT).
Oakland, California and other locations
Our lead scientists for Alpha Thalassemia research studies include Tippi C MacKenzie, MD.
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