RGX-121 Gene Therapy in Children 5 Years of Age and Over With MPS II (Hunter Syndrome)
Summary
- Eligibility
- for males ages 5-17 (full criteria)
- Location
- at Oakland, California and other locations
- Dates
- study startedestimated completion
- Principal Investigator
- by Paul Harmatz
Description
Summary
Official Title
Details
Keywords
Eligibility
Locations
Lead Scientist at UCSF
- Paul Harmatz
Professor, Pediatrics, School of Medicine. Authored (or co-authored) 205 research publications
Details
- Status
- accepting new patients
- Start Date
- Completion Date
- (estimated)
- Sponsor
- REGENXBIO Inc.
- ID
- NCT04571970
- Phase
- Phase 1/2 research study
- Study Type
- Interventional
- Participants
- Expecting 6 study participants
- Last Updated