Vision Disorders clinical trials at UCSF
2 in progress, 1 open to eligible people
Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
open to eligible people ages 6 years and up
The purpose of this double-masked, randomized, placebo-controlled, paired-eye study is to evaluate the efficacy, safety and tolerability of Sepofarsen in subjects with Leber Congenital Amaurosis (LCA) due to the c.2991+1655A>G (p.Cys998X) mutation in the CEP290.
San Francisco, California and other locations
Ultevursen in Subjects With Retinitis Pigmentosa (RP) Due to Mutations in Exon 13 of the USH2A Gene
Sorry, in progress, not accepting new patients
The purpose of this Phase 2b study is to evaluate the safety and tolerability of ultevursen administered via intravitreal injection (IVT) in subjects with Retinitis Pigmentosa (RP) due to mutations in exon 13 of the USH2A gene. This is a multicenter Double-masked, Randomized, Sham-controlled study which will enroll 81 subjects.
San Francisco, California and other locations
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