Wolman Disease clinical trials at UCSF

1 in progress, 0 open to eligible people

In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases
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The investigators aims to determine the the maternal and fetal safety and feasibility of in utero fetal enzyme replacement therapy in fetuses with Lysosomal Storage Diseases.
San Francisco, California

Last updated: August 25, 2020