This study is accepting new patients by invitation only
Patients Treated for SCID (1968-Present)
Summary
- Location
- at San Francisco, California and other locations
- Dates
- study startedestimated completion
- Principal Investigator
- by Morton J. Cowan, MD
Description
Summary
Official Title
Details
Keywords
Eligibility
Locations
Lead Scientist at UCSF
- Morton J. Cowan, MD
TR3-05535 Cowan (PI) 11/01/2012-10/31/2015 California Institute of Regenerative Medicine vGene Correction of Autologous Hematopoietic Stem Cells in Artemis Deficient SCID Goal is to complete the preclinical testing necessary for a clinical gene therapy trial in children with Artemis-SCID.
Details
- Status
- accepting new patients by invitation only
- Start Date
- Completion Date
- (estimated)
- Sponsor
- National Institute of Allergy and Infectious Diseases (NIAID)
- Links
- Primary Immune Deficiency Treatment Consortium (PIDTC) Division of Allergy, Immunology, and Transplantation (DAIT) National Institute of Allergy and Infectious Diseases (NIAID) National Center for Advancing Translational Sciences (NCATS)
- ID
- NCT01346150
- Study Type
- Observational
- Participants
- Expecting 1007 study participants
- Last Updated