Natural History Study of SCID Disorders
a study on Severe Combined Immunodeficiency Leaky SCID Reticular Dysgenesis ADA Deficiency X-Linked Severe Combined Immunodeficiency
Summary
- Location
- at San Francisco, California and other locations
- Dates
- study startedestimated completion
- Principal Investigator
- Christopher C. Dvorak, MDMorton J. Cowan, MD
Description
Summary
Official Title
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Eligibility
Locations
Lead Scientists at UCSF
- Christopher C. Dvorak, MD
My Research Interests are divided into 3 areas of focus: 1. Supportive Care (especially Invasive Fungal Infections) following Hematopoietic Stem Cell Transplantation 2. Transplantation for Severe Combined Immunodeficiency 3. - Morton J. Cowan, MD
California Institute of Regenerative Medicine vGene Correction of Autologous Hematopoietic Stem Cells in Artemis Deficient SCID Goal is to complete the preclinical testing necessary for a clinical gene therapy trial in children with Artemis-SCID.
Details
- Status
- accepting new patients
- Start Date
- Completion Date
- (estimated)
- Sponsor
- National Institute of Allergy and Infectious Diseases (NIAID)
- Links
- Primary Immune Deficiency Treatment Consortium (PIDTC) featured highlights
- Division of Allergy, Immunology, and Transplantation (DAIT)
- National Institute of Allergy and Infectious Diseases (NIAID)
- Rare Diseases Clinical Research Network (RDCRN)
- National Center for Advancing Translational Science (NCATS)
- ID
- NCT01186913
- Study Type
- Observational
- Last Updated