This study is accepting new patients by invitation only
Natural History Study of SCID Disorders
Summary
- Location
- at San Francisco, California and other locations
- Dates
- study startedcompletion around
- Principal Investigator
- by Christopher C. Dvorak, MDMorton J. Cowan, MD
Description
Summary
Official Title
Details
Keywords
Eligibility
Locations
Lead Scientists at UCSF
- Christopher C. Dvorak, MD
My Research Interests are divided into 3 areas of focus: 1. Supportive Care (especially Invasive Fungal Infections) following Hematopoietic Stem Cell Transplantation 2. Transplantation for Severe Combined Immunodeficiency 3. Transplantation for Rare Leukemias (JMML and APL) - Morton J. Cowan, MD
TR3-05535 Cowan (PI) 11/01/2012-10/31/2015 California Institute of Regenerative Medicine vGene Correction of Autologous Hematopoietic Stem Cells in Artemis Deficient SCID Goal is to complete the preclinical testing necessary for a clinical gene therapy trial in children with Artemis-SCID.
Details
- Status
- accepting new patients by invitation only
- Start Date
- Completion Date
- (estimated)
- Sponsor
- National Institute of Allergy and Infectious Diseases (NIAID)
- Links
- Primary Immune Deficiency Treatment Consortium (PIDTC) featured highlights Rare Diseases Clinical Research Network (RDCRN) National Center for Advancing Translational Science (NCATS)
- ID
- NCT01186913
- Study Type
- Observational
- Participants
- Expecting 690 study participants
- Last Updated